The GM2 gangliosidoses: Unlocking the mysteries of pathogenesis and treatment
[摘要]
[发布日期] 2021-11-01 [发布机构]
[效力级别] [学科分类]
[关键词] GM2;Gangliosidoses;Tay-Sachs disease;Sandhoff disease;Hexosaminidase A;HEXA;HEXB;Lysosomal storage diseases;Gene therapy [时效性]
